November 15, 2024 - 10:54
One of the key hurdles in developing effective gene therapies for these disorders is the large size of the genes that need to be delivered into the patient's cells. Traditional gene delivery methods often struggle with this, limiting their effectiveness. Consequently, researchers are exploring innovative technologies to overcome these limitations.
Advanced delivery systems are being developed to ensure that larger genes can be effectively transported into the target cells. These systems aim to enhance the stability and efficiency of the gene transfer process, paving the way for more effective treatments for muscular dystrophy.
As the field of gene therapy continues to evolve, the hope is that these advancements will lead to successful interventions for individuals affected by muscular dystrophies, improving their quality of life. The focus remains on refining delivery mechanisms and enhancing the therapeutic potential of gene therapy, ultimately aiming to address the challenges posed by the size of the genes involved in these debilitating conditions.
